Where can I buy the new drug deflazacort for Duchenne muscular dystrophy? How to use?

Duchenne muscular dystrophy (DMD) is caused by mutations in the dystrophin gene. It is an X-chromosome recessive genetic disease that affects one in every 3,500 newborn boys worldwide. It is the world's first corticosteroid drug approved to treat DMD. Today let’s take a closer look at where to buy Deflazacort? How to use?

Deflazacort has been approved by the U.S. Food and Drug Administration (FDA) for the treatment of Duchenne muscular dystrophy (DMD) patients aged 5 years and above. Currently, the drug is not available in mainland China. Patients cannot buy this drug in hospital pharmacies. Patients in need can purchase it abroad or obtain it through domestic professional overseas medical service organizations (such as Medical Companion Travel). The price is very affordable through direct mail from overseas pharmaceutical factories. It is suitable for patients to take medicine for a long time, which can reduce a lot of financial burden. It is convenient and fast to buy medicines without going abroad. However, drug prices are constantly changing due to exchange rate fluctuations. It is recommended to consult the medical companion passenger service staff for specific drug prices and drug purchase procedures.

The therapeutic effect of deflazacort is significant, and patients need to take the medication as directed by their doctor. Adults and children 2 years and older: oral deflazacort 0.9 mg/kg/day daily; if tablets are used, any combination of tablet strengths can be used to achieve the calculated dose; safety and effectiveness in children under 2 years of age have not been established. When discontinuing treatment, gradually reduce the dose if administered for more than a few days. Patients who are allergic to any of the inactive ingredients of deflazacort are contraindicated. Pay attention to the side effects of this drug, including cough, frequent urination, weight gain, increased appetite, upper respiratory tract infection, etc. Patients should not change the dosage and usage at will to avoid intolerance reactions.

Note: The above information comes from the Internet and is compiled and edited by Medical Companion Travel (please correct me if there are any errors or omissions). It is only to provide information on the latest drugs on the market in the world and help Chinese patients understand the latest international new drug trends. It is only for internal discussion among medical staff and does not serve as any basis for medication. For specific medication guidelines, please consult the attending physician.

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